FORMERLY KNOWN AS SOFIA SEES HOPE
SEEING A CURE FOR BLINDNESS
What is Leber Congenital Amaurosis (LCA)?
LCA is a rare inherited retinal disease characterized by severe vision loss at birth. While some children are born with little or no vision, others may have significant vision loss in the first few years of life, stable vision for a period of time, and then eventually complete vision loss as the retina deteriorates into total blindness.
What We Do
Founded in 2014 as Sofia Sees Hope, Hope in Focus is a nonprofit 501(c)3 patient advocacy organization dedicated to generating awareness, raising funds for research, and providing support, education and outreach to the LCA and rare inherited retinal disease community.
Thank You to These Organizations
for their Ongoing Commitment to Hope in Focus.
Let’s Get Social!
➡️ Dr. Michaelides emphasizes that finding new #LCA treatments and cures fundamentally depends on the voices of patients. ⬅️![]()
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Get a glimpse of the ophthalmic work in progress at MeiraGTx, a clinical-stage gene therapy company headquartered in New York and London. ![]()
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The biotech focuses on developing potential curative treatments for patients living with serious diseases, including IRDs and Age-Related Macular Degeneration. ⬇
Let's Chat About...Gene Therapy News for LCA13, LCA1, LCA2, and LCA4 - Hope in Focus
hopeinfocus.org
One of Britain's top ophthalmologists delivers promising gene therapy research news for multiple forms of Leber congenital amaurosis (LCA).
Naomi is a student at Virginia School for the Deaf and Blind, a #BrailleChallenge finalist, and a #filmmaker. She also lives with one of the rarest forms of Leber congenital amaurosis – LCA5.![]()
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Knowing how eager she is for total independence, Namoi’s parents would do anything to find a cure for their daughters' #VisualImpairment. Especially so she could drive her own car. ![]()
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The #GoodNews? Opus Genetics has filed for a new research program which prioritizes finding a cure for this severe form of #LCA. Read the full story! ⬇![]()
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hopeinfocus.org/family-excited-about-new-lca5-lebercilin-research-program/
Family Excited About New LCA5-Lebercilin Research Program - Hope in Focus
hopeinfocus.org
Family living with LCA5-Lebercilin excited about retinal clinical research prospects on one of the rarest forms of Leber congenital amaurosis.