FORMERLY KNOWN AS SOFIA SEES HOPE

SEEING A CURE FOR BLINDNESS

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What is Leber Congenital Amaurosis (LCA)?

LCA is a rare inherited retinal disease characterized by severe vision loss at birth. While some children are born with little or no vision, others may have significant vision loss in the first few years of life, stable vision for a period of time, and then eventually complete vision loss as the retina deteriorates into total blindness.

What is LSA?

What is Leber Congenital Amaurosis (LCA)?

LCA is a rare inherited retinal disease characterized by severe vision loss at birth. While some children are born with little or no vision, others may have significant vision loss in the first few years of life, stable vision for a period of time, and then eventually complete vision loss as the retina deteriorates into total blindness.

What We Do

Founded in 2014 as Sofia Sees Hope, Hope in Focus is a nonprofit 501(c)3 patient advocacy organization dedicated to generating awareness, raising funds for research, and providing support, education and outreach to the LCA and rare inherited retinal disease community.

Thank You to These Organizations

for their Ongoing Commitment to Hope in Focus.

 
Editas
ProQR
Spark
Simply Majestic
Dominion
agtc
MeiraGTx
Janssen
 

Let’s Get Social!

16 hours ago

Hope in Focus
Have you seen our latest news? Join our mailing list and get your own FREE printed copy of our periodic newsletter or download the digital version of this month's edition or any of our past publications here > hopeinfocus.org/resources/newsletter/Image description: Front of June newsletter with Hope in Focus logo at the top and two articles with photos below. ... See MoreSee Less
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3 days ago

Hope in Focus
"MeiraGTx Announces Positive Top-Line Data from the MGT009 Phase 1/2 Clinical Study Demonstrating Safety and Improvement in Multiple Domains of Vision in X-Linked Retinitis Pigmentosa Patients treated with Botaretigene Sparoparvovec (AAV-RPGR) compared to Untreated Randomized Control" investors.meiragtx.com/news-releases/news-release-details/meiragtx-announces-positive-top-line-da... ... See MoreSee Less
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