January 2022 - Hope in Focus

Posted January 28, 2022

Let’s Chat About…ProQR’s Work in Treatments for Inherited Retinal Disease

ProQR Therapeutics’ Founder and Chief Executive Officer shared exciting news of the deep pipeline of RNA therapies in development to treat Leber congenital amaurosis (LCA) and other [...]

Let’s Chat About…Gene Therapy News for LCA13, LCA1, LCA2, and LCA4

One of Britain’s top ophthalmologists delivered promising research news on several forms of Leber congenital amaurosis, including LCA13 (RDH12), LCA1 (GUCY2D), LCA2 (RPE65), and LCA4 (AIPL1). [...]

Family Excited About New LCA5-Lebercilin Research Program

John Mills says he would crawl over broken glass if it led to a cure for his daughter’s visual impairment caused by one of the rarest of rare inherited retinal […]