Let’s Chat About…ProQR’s Work in Treatments for Inherited Retinal Disease
ProQR Therapeutics’ Founder and Chief Executive Officer shared exciting news of the deep pipeline of RNA therapies in development to treat Leber congenital...
Science Education
Let’s Chat About … CRISPR and Gene Editing
For the first time, early research data shows that a gene editing technique called CRISPR improved vision in people living...
Let’s Chat About … the Importance of the Patient Voice in Rare Disease
We hear a lot these days about the necessity of the patient voice in developing treatments, especially for people living...
Let’s Chat About … Patient Registries and My Retina Tracker
Join the My Retina Tracker® registry and you’ll be contributing to science by driving research to help improve your quality of...
Let’s Chat About … Why Natural History and Patient Outcome Studies Matter
Amid the intricacies of researching treatments and cures for rare diseases, such as Leber congenital amaurosis (LCA) and other inherited retinal diseases (IRDs), the...
Let’s Chat About … Genetics and Inherited Retinal Disease
You or your loved one just received a clinical diagnosis of Leber congenital amaurosis (LCA), a rare inherited retinal disorder caused by...
“Let’s Chat About …” Webinar Provides Insight Into How the FDA Handles Rare Disease Treatments
Researchers and regulators did not miss a single step in the fast-tracked federal process of developing successful COVID-19 vaccines. And the...
‘Let’s Chat About …’ Webinar Offers LCA Overview and Updates on Clinical Trials
In the debut of Hope in Focus (formally Sofia Sees Hope) ‘Let’s Chat About …’ monthly webinar series, Ben Shaberman of the Foundation Fighting Blindness,...
Reflecting on the Trajectory of IRD Research
When I joined the Foundation Fighting Blindness as a science writer in 2004, I really didn’t know what I was...
Clinical Trials and Emerging Research Show Promise for LCA Treatments
Forty clinical trials and a lot of pre-clinical research into LCA treatments show promising pathways to discovering the next LUXTURNA®, according...